The potential of gene therapies is finally being realized and these therapies can deliver life-changing treatments for a broad range of disorders.

Building on Atuka’s pioneering work in Parkinson’s disease and other neurodegenerative disorders, this paper lays out the transformative potential of gene therapy, covering critical advancements and future directions in the field.

Lately, we have leveraged our expertise in rodent and non-human primate (NHP) neuroanatomy and neurosurgery to become experts at delivering pharmacodynamic and biodistribution studies in the gene therapy area.

Whether you’re a researcher, clinician, pharmaceutical leader, or biotech enthusiast, here Patrick Howson provides valuable insights into the preclinical development of gene therapies, focusing on innovative delivery methods, regulatory landscapes, and evolving market dynamics.

Join us in exploring how gene therapy is revolutionizing medicine and offering new hope for countless patients worldwide.

• Advanced Delivery Systems: Explore the cutting-edge techniques improving gene therapy delivery, including rAAV vectors and non-viral platforms.
• Regulatory Challenges: Navigate the complex and fragmented regulatory landscape that gene therapies navigate.
• Market Insights: Understand the current market and future trends driving the growth of gene therapies.
• Preclinical Development: Learn about the crucial preclinical considerations, from species selection to immunogenicity and genomic risks.